Rare Diseases Research Challenges Call for proposals

28 April 2020

The French Foundation for Rare Diseases, partner of the European Joint Programme for Rare Diseases EJPRD, is pleased to announce the launch of the Rare Diseases Research (RDR) Challenges call.

The main objective of this innovative call is to facilitate and fund collaborative projects between industry, academia, SMEs and patient organisations to solve specific research challenges in the field of therapeutic development.

The total budget of 1,5 M€ will allow 4 projects to be funded. Once selection of projects is completed, the industry sponsors who were involved in the challenges definition, will join and co-fund the granted projects.

The 4 Challenges and their sponsors are:

Challenge 1: Development of a non-invasive tool for measuring rare disease patient mobility in daily living. Sponsors: Chiesi Farmaceutici S.p.A. (Italy), CSL Behring

Challenge 2: Delivery system for intranasal administration of biological drugs to neonates. Sponsor: Chiesi Farmaceutici S.p.A. (Italy)

Challenge 3: Characterize Rare Bone Disorders (RBD) Mobility Challenges in Real World Setting.
Sponsor: Ipsen

Challenge 4: Pre-clinical assay to detect instability of microsatellite repeat expansions.
Sponsors: Pfizer, Cydan

The consortium submitting an application for a RDR Challenge budget must involve a minimum of two eligible applicants: researchers and/or health care professionals
and/or SME(s) and/or patient advocacy organization(s), from at least two different countries participating in the EJP RD at the time of the application. The maximum duration of the project is 30 months, with first milestones/deliverables at 18 months.

Deadline : June 30th, 2PM CEST.

online submission